Diseases

This list is not all-inclusive and may contain some diseases for which transplants are no longer performed. There may also be omissions of diseases for which transplants are currently the prescribed form of treatment. Please consult a health care professional for questions about a specific disease. You can also make inquiries through our Ask the Expert program.

Acute Lymphoblastic Leukemia (ALL)
Acute Myelogenous Leukemia (AML)
Adenoleukodystrophy (ALD)
Agnogenic Myeloid Metaplasia (Myelofibrosis)
AL Amyloidosis
Amegakaryocytosis/Congenital Thrombocytopenia
Anaplastic Astrocytoma
Astrocytomas
Beta Thalassemia Major
Chronic Granulomatous Disease (CGD)
Chronic Lymphocytic Leukemia (CLL)
Chronic Myelogenous Leukemia (CML)
Chronic Myelomonocytic Leukemia (CMML)
Clear Cell Sarcoma
Desmoplastic Small Round Cell Tumor
Diamond-Blackfan Anemia (DBA)
Ependymomas
Ewing’s Sarcoma
Familial Erythrophagocytic Lymphohistiocytosis
Fanconi Anemia
Germ Cell Tumor
Griscelli Syndrome Type II
Hemophagocytic Lymphohistiocytosis (HLH)
Hepatoblastoma
Hodgkin’s Lymphoma (Hodgkin’s Disease)
Hurler’s Syndrome (MPS IH)
Juvenile Chronic Myelogenous Leukemia (JCML)
Juvenile Myelomonocytic Leukemia (JMML)
Kostmann Syndrome
Krabbe Disease
Maroteaux-Lamy Syndrome (MPS VI)
Medulloblastoma
Metachromatic Leukodystrophy
Mixed Gliomas
Multiple Myeloma (Kahler disease)
Neuroblastoma
Non-Hodgkin’s Lymphoma
Oligodendrogliomas
Osteogenesis Imperfecta
Osteosarcoma
Paroxysmal Nocturnal Hemoglobinuria (PNH)
POEMS Syndrome
Primitive Neuroectodermal Tumor
Pure Red Cell Aplasia
Refractory Anemia (RA), all types
Renal Cell Carcinoma
Retinoblastoma
Rhabdomyosarcoma
Severe Aplastic Anemia
Severe Combined Immunodeficiency (SCID), all sub-types
SCI
Sickle Cell Disease
Sly Syndrome (MPS VII)
Thalassemia
Wilms’ Tumor
Wiskott-Aldrich Syndrome